Rare/orphan diseases

Rare or orphan diseases can be inherited and may only affect a relatively small population worldwide. Or they can be rare forms of acquired diseases that span other therapeutic areas such as respiratory, oncology, inflammation and infectious diseases.

Rare/orphan diseases

A number of clients specialise in finding life-changing medicines for rare/orphan diseases that may be poorly served by current medications.

Such diseases are often targeted by the emerging biotech companies who make up the majority of our customers.

Inhouse expert teams

We are experienced in working with companies in the orphan/rare disease space and understand the needs of this sector.

This can include collaborating with partners to access specific sources of funding (such as grants) and where necessary, exploring flexible deal structures to ensure mutual success.

Our success stories

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